# Bioblast Pharma

**URL:** <https://forum.livingwithataxia.org/t/bioblast-pharma/5229>\
**Category:** News, Research, and Clinical Trials\
**Created:** [September 3, 2016, 9:28pm UTC](https://forum.livingwithataxia.org/t/bioblast-pharma/5229 "2016-09-03T21:28:16Z")\
**Posts on this page:** 3\
**Page:** 1

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**Author:** ![jman](https://yyz1.discourse-cdn.com/flex027/user_avatar/forum.livingwithataxia.org/jman/32/3523_2.png) [@jman](https://forum.livingwithataxia.org/u/jman)\
**Post date:** [September 3, 2016, 9:28pm UTC](https://forum.livingwithataxia.org/t/bioblast-pharma/5229/1 "2016-09-03T21:28:16Z")

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This is some great research in SCA3 out of Jeruselem. They are developing drugs for MJD patients. Wow this is great news. Can those of you with anymore info please chime in. In the mean time please visit [https://bioblastpharma.com](https://bioblastpharma.com) and do a search for SCA3

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**Author:** ![ataxiabr](https://yyz1.discourse-cdn.com/flex027/user_avatar/forum.livingwithataxia.org/ataxiabr/32/1826_2.png) [@ataxiabr](https://forum.livingwithataxia.org/u/ataxiabr)\
**Post date:** [September 8, 2016, 1:31pm UTC](https://forum.livingwithataxia.org/t/bioblast-pharma/5229/2 "2016-09-08T13:31:30Z")

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That’s a little hope for us @jman. Thanks!

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**Author:** ![ataxiabr](https://yyz1.discourse-cdn.com/flex027/user_avatar/forum.livingwithataxia.org/ataxiabr/32/1826_2.png) [@ataxiabr](https://forum.livingwithataxia.org/u/ataxiabr)\
**Post date:** [September 8, 2016, 2:37pm UTC](https://forum.livingwithataxia.org/t/bioblast-pharma/5229/3 "2016-09-08T14:37:46Z")

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If you want to follow their study you can check [here](https://clinicaltrials.gov/ct2/show/NCT02147886?term=sca3&rank=7).
